I am a paediatric haematologist specialized in sickle cell disease, the most common genetic disorder worldwide.
The lack of standardized and patient-centred outcomes is a major obstacle to the development of new drugs, while therapeutic options remain limited.
To address this issue, my objective is to develop a core outcome set specific to sickle cell disease, focused on the concerns of children living in both high- and low-income countries.
That is why I joined the METHODS team within the CRESS unit to pursue a PhD.
Theses
Towards standardized and patient-centered therapeutic research in sickle cell disease
Marica Rossi
Promotion : 2025
Supervisor.s : Brigitte Ranque
