I am a paediatric haematologist specialized in sickle cell disease, the most common genetic disorder worldwide.
The lack of standardized and patient-centred outcomes is a major obstacle to the development of new drugs, while therapeutic options remain limited.
To address this issue, my objective is to develop a core outcome set specific to sickle cell disease, focused on the concerns of children living in both high- and low-income countries.
That is why I joined the METHODS team within the CRESS unit to pursue a PhD.
Research interests
- Sickle cell disease
- Patient reported outcomes
- Core outcome set
Key publications
- Rossi M, Belinga S, Tolo A, Diop S, Diagne I, Chelo D, Wamba G., Gonzalez J-P, Abough'elie C, Traore Y, Deme-ly I, Seck M, Diaw M, Gbonon V, Boidy K, Kamara I, Kitenge R, Jouven X, Tshilolo L, Diallo D, Ranque B. Determinants of the haemoglobin level in patients with sickle cell disease living in sub‐Saharan Africa: Major impact of the country of residence and independent effects of leucocyte and platelet counts and haemolysis. Br J Haematol. 2024;205(2):664–673. https://doi.org/10.1111/ bjh.19576
View publication - Rossi M, Szepetowski S, Yakouben K, Paillard C, Sirvent A, Castelle M, Pegon C, Piguet C, Grain A, Angoso M, Robin M, Dhedin N, Pondarré C, Dumesnil de Maricourt C, Berceanu A, Simon P, Marcais A, Poirée M, Gandemer V, Plantaz D, Nguyen S, Michel G, Loundou A, Dalle J-H and Thuret I. Recent results of hematopoietic stem cell transplantation for thalassemia with busulfan-based conditioning regimen in France: improved thalassemia free survival despite frequent mixed chimerism. A retrospective study from the Francophone Society of Stem Cell Transplantation and Cellular Therapy (SFGM-TC). Bone Marrow Transplant. 2023;58(11):1254-1256. doi: 10.1038/s41409-023-02079-0
View publication - Rossi M, Pirenne F, Le Roux E, Smaïne D, Belloy M, Eyssette‐Guerreau S, Couque N, Holvoet L, Ithier G, Brousse V, Koehl B, Faye A, Benkerrou M, Missud F. Delayed haemolytic transfusion reaction in paediatric patients with sickle cell disease: A retrospective study in a French national reference centre. Br J Haematol. 2023 ;201(1):125-132. doi: 10.1111/bjh.18605
View publication
Links
Theses
Towards standardized and patient-centered therapeutic research in childhood sickle cell disease: international development of a minimal set of outcome measures (core outcome set)
Marica Rossi
Promotion : 2025
Supervisor.s : Brigitte Ranque
